Gene Therapy Basics (2022 Update)
A gene therapy platform for treating diseases
Boy with ultra-rare disease begins groundbreaking gene therapy
Gene Therapy and Sickle Cell Disease
Gene Therapy for Inherited Retinal Diseases
What types of diseases could gene therapy treat?
How Gene Therapy is Changing the Future of Medicine
Gene Therapy: What Does It Mean for Rare Disease Communities?
Gene Therapy - Treating the Disease Instead of the Symptoms | Tomorrow Today
NIH SciBites From Home: Developing Gene Therapies for Genetic Diseases
Gene Therapy
Gene therapy: Young child gets treatment for Sandhoff disease
Gene Therapy 101: What Is It and How Can It Help Us Treat Rare Genetic Disorders?
Radical new gene therapy restores sight to patients with rare eye condition - BBC News
The Cost of Gene Therapy in Treating Sickle Cell Disease
Patients respond to gene therapy treatment for sickle cell anemia
The First CRISPR Gene Therapy Is Here
New gene-therapy technique, MyoAAV, may improve treatment of certain muscle diseases
Gene Therapy for the Treatment of Hemophilia B: Andrew M. Davidoff, MD at TEDxSonomaCounty
How Can We Make Gene Therapy Effective and Affordable?