Huntington's Disease: Can Gene Therapy Help?

Boy with ultra-rare disease begins groundbreaking gene therapy

Gene Therapy for Inherited Retinal Diseases

Gene Therapy 101: What Is It and How Can It Help Us Treat Rare Genetic Disorders?

Radical new gene therapy restores sight to patients with rare eye condition - BBC News

NIH SciBites From Home: Developing Gene Therapies for Genetic Diseases

Gene Therapy Basics (2022 Update)

What types of diseases could gene therapy treat?

How Metabolic Therapy CHECKMATES Cancer

Here’s how gene therapy for sickle cell disease could help provide functional cure for patients

Gene therapy into brain helps kid with rare disease

Gene Therapy Inside Out

The First CRISPR Gene Therapy Is Here

Clinical Trial Tests Gene Therapy as Treatment of Sickle Cell Disease

Can we cure genetic diseases by rewriting DNA? | David R. Liu

Gene Therapy: What Does It Mean for Rare Disease Communities?

How Gene Therapy is Changing the Future of Medicine

Gene therapy is the future of medicine - here's how | Dr. Nafiseh Nafissi | TEDxToronto

Gene Therapy

Pompe Disease and Gene Therapy